Jayne DR, Merkel PA, Yue H, et al.
Complement C5a Receptor Inhibitor Avacopan Improves Renal Function in
ANCA Vasculitis
ASN Annual Meeting 2020 -- Digital Meeting
J Am Soc Nephrol
(Oct) 31:53A 2020

BACKGROUND
Renal impairment is common in anti-neutrophil
cytoplasmic autoantibody-associated vasculitis. The resulting chronic kidney
disease and exacerbation of the toxicity risks of high dose or prolonged
glucocorticoid use, a mainstay of ANCA treatment, are major consequences.
Avacopan was tested for efficacy and effects on renal function compared to
standard prednisone therapy in a randomized double-blind Phase 3 trial in
ANCA vasculitis.
METHODS
Subjects randomized 1:1 received
either prednisone (60 mg tapered to 0 over 20 weeks) or avacopan (30 mg twice
daily for 52 weeks), combined with either cyclophosphamide
(CYC) followed by azathioprine, or rituximab (RTX).
Primary endpoints: Disease remission at week 26 and sustained remission at
week 52. Changes in urinary albumin to creatinine ratio (UACR) and estimated
glomerular filtration rate (eGFR) were also
assessed.
RESULTS
330 subjects were treated: 166 to avacopan
and 164 to prednisone treatment groups. Avacopan remission at week 26 was
72.3% vs. 70.1%, for prednisone (P<0.0001 for non-inferiority); avacopan
was superior to prednisone for sustained remission (week 52, 65.7%, avacopan
vs. 54.9%, prednisone, P=0.0066).
81% percent of subjects had renal
disease. UACR decreased more rapidly with avacopan than prednisone: week 4
avacopan was 40% below baseline vs. no change for prednisone (P<0.0001).
Baseline to week 52 eGFR (mL/min/1.73 m2) improvement: avacopan
eGFR +7.3 vs. prednisone +4.1 (P=0.029). In subjects with baseline eGFR
<30: mean eGFR improved 67% more with avacopan than prednisone to week 52:
avacopan eGFR +13.7 vs. prednisone +8.2
(P=0.01).
CONCLUSION
Treatment with avacopan for ANCA
vasculitis compared with standard glucocorticoid therapy (both combined with
either CYC or RTX) is as effective for remission induction at 26 weeks, and
superior to prednisone for sustained remission after 52 weeks. Avacopan led
to faster falls in UACR and greater recovery in eGFR when compared to
standard prednisone therapy. These findings have important implications for
the long term health of AAV patients through better overall disease control,
reduced prednisone exposure and reduced severity of chronic kidney
disease.

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